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Study Details

A new drug combination study in children with Infantile-Onset Pompe Disease

(IRB#: IRB_00147223)

The goal of this study is to see if a new drug combination can help children with Pompe Disease. The two drugs in the combination are called cipaglucosidase alfa (ATB200) and miglustat (AT2221). This study will also see how safe this drug combination is.

I AM INTERESTED

  • All genders
  • All Ages
  • Volunteers with special conditions
  •   In Person
  • Paid

Who can participate?

 Gender: All genders

  Age: All Ages

  Volunteers: Volunteers with special conditions

   Location: In Person

Will I be paid for my time?

Yes

For more information contact:

Carrie Bailey

carrie.bailey@hsc.utah.edu

  8015873605

IRB#: IRB_00147223

PI: David Viskochil

Department: PEDIATRIC GENETICS

Approval Date: 2023-08-09 06:00:00

Specialties: Pediatric Genetics

Last Updated: 6/8/23